OHSU scientists unlock first critical step toward gene therapy treatment for patients with mitochondrial disease

Gene-based cures for human diseases are now on the horizon

July 15, 2015 Portland, Ore.

Fibroblasts derived from mitochondrial patients, 2015. (OHSU)

Stem cell colonies growing on top of feeder cells. (OHSU)

Stem cell colonies growing on top of feeder cells with immunochemistry staining. (OHSU)

An image used in the Nature paper, showing neuronal progenitor cells differentiated from SCNT-ESC cells. (OHSU)

Shoukhrat Mitalipov, Ph.D., 2013. (OHSU)

Hong Ma, M.D., Ph.D., 2015. (OHSU)